Widespread correction of brain pathology in feline alpha-mannosidosis by dose escalation of intracisternal AAV vector injection

Autor: Hunter, Jacqueline E., Molony, Caitlyn M., Bagel, Jessica H., O’Donnell, Patricia, Vite, Charles H., Chawla, Sanjeev, Poptani, Harish, Wolfe, John H.
Zdroj: In Molecular Therapy - Methods & Clinical Development 13 June 2024 32(2)
Databáze: ScienceDirect