Widespread correction of brain pathology in feline alpha-mannosidosis by dose escalation of intracisternal AAV vector injection

Autor: Hunter, Jacqueline E. 1, Molony, Caitlyn M. 2, Bagel, Jessica H. 2, O’Donnell, Patricia 2, Vite, Charles H. 2, Chawla, Sanjeev 3, Poptani, Harish 4, Wolfe, John H. 1, 2, 5, ∗
Zdroj: In Molecular Therapy - Methods & Clinical Development 13 June 2024 32(2)
Databáze: ScienceDirect