A 3-month gene therapy single-dose IV administration pharmacology and safety study with ST-920 (isaralgagene civaparvovec) for Fabry disease in mice

Autor: Meyer, Kathleen E., Lorget, Florence, Prawdzik, Gregg, Falaleeva, Marina, Cao, Liching, Falese, Lillian, Huston, Marshall W., Hettini, Khaled, Lu, Yanmei, Ledeboer, Annemarie
Zdroj: In Molecular Genetics and Metabolism February 2024 141(2)
Databáze: ScienceDirect
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