A 3-month gene therapy single-dose IV administration pharmacology and safety study with ST-920 (isaralgagene civaparvovec) for Fabry disease in mice

Autor: Meyer, Kathleen E. a, Lorget, Florence b, Prawdzik, Gregg c, Falaleeva, Marina a, Cao, Liching a, Falese, Lillian d, Huston, Marshall W. e, Hettini, Khaled a, Lu, Yanmei a, Ledeboer, Annemarie a
Zdroj: In Molecular Genetics and Metabolism February 2024 141(2)
Databáze: ScienceDirect