Gene Transfer of Human Acid Sphingomyelinase Corrects Neuropathology and Motor Deficits in a Mouse Model of Niemann-Pick Type A Disease

Autor: Yang, Wendy, Schuchman, Edward H., Cheng, Seng H., Shihabuddin, Lamya S., Stewart, Gregory R.
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2005 Dec 01. 102(49), 17822-17827.
Databáze: JSTOR Journals