Bifunctional Antisense Oligonucleotides Provide a Trans-Acting Splicing Enhancer That Stimulates SMN2 Gene Expression in Patient Fibroblasts

Autor:	Skordis, Leigh A., Dunckley, Matthew G., Yue, Baigong, Eperon, Ian C., Muntoni, Francesco
Zdroj:	Proceedings of the National Academy of Sciences of the United States of America, 2003 Apr 01. 100(7), 4114-4119.
Databáze:	JSTOR Journals
Externí odkaz:	https://www.jstor.org/stable/3148749 Zobrazit plný text záznamu