Combination therapy utilizing shRNA knockdown and an optimized resistant transgene for rescue of diseases caused by misfolded proteins

Autor: Li, Chengwen, Xiao, Pingjie, Gray, Steven James, Weinberg, Marc Scott, Samulski, R. Jude
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2011 Aug . 108(34), 14258-14263.
Databáze: JSTOR Journals