Combination therapy utilizing shRNA knockdown and an optimized resistant transgene for rescue of diseases caused by misfolded proteins
Autor: | Li, Chengwen, Xiao, Pingjie, Gray, Steven James, Weinberg, Marc Scott, Samulski, R. Jude |
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Zdroj: | Proceedings of the National Academy of Sciences of the United States of America, 2011 Aug . 108(34), 14258-14263. |
Databáze: | JSTOR Journals |
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