Precise small-molecule cleavage of an r(CUG) repeat expansion in a myotonic dystrophy mouse model

Autor: Angelbello, Alicia J., Rzuczek, Suzanne G., Mckee, Kendra K., Chen, Jonathan L., Olafson, Hailey, Cameron, Michael D., Moss, Walter N., Wang, Eric T., Disney, Matthew D.
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2019 Apr . 116(16), 7799-7804.
Databáze: JSTOR Journals