Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector

Autor:	Cideciyan, Artur V., Sudharsan, Raghavi, Dufour, Valérie L., Massengill, Michael T., Iwabe, Simone, Swider, Malgorzata, Lisi, Brianna, Sumaroka, Alexander, Marinho, Luis Felipe, Appelbaum, Tatyana, Rossmiller, Brian, Hauswirth, William W., Jacobson, Samuel G., Lewin, Alfred S., Aguirre, Gustavo D., Beltran, William A.
Zdroj:	Proceedings of the National Academy of Sciences of the United States of America, 2018 Sep 01. 115(36), E8547-E8556.
Databáze:	JSTOR Journals
Externí odkaz:	https://www.jstor.org/stable/26531255 Zobrazit plný text záznamu