PTC124 Is an Orally Bioavailable Compound That Promotes Suppression of the Human CFTR-G542X Nonsense Allele in a CF Mouse Model

Autor: Du, Ming, Liu, Xiaoli, Welch, Ellen M., Hirawat, Samit, Peltz, Stuart W., Bedwell, David M.
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2008 Feb 01. 105(6), 2064-2069.
Databáze: JSTOR Journals