RNAi-mediated silencing of hepatic Alas1 effectively prevents and treats the induced acute attacks in acute intermittent porphyria mice

Autor: Yasuda, Makiko, Gan, Lin, Chen, Brenden, Kadirvel, Senkottuvelan, Yu, Chunli, Phillips, John D., New, Maria I., Liebow, Abigail, Fitzgerald, Kevin, Querbes, William, Desnick, Robert J.
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2014 May . 111(21), 7777-7782.
Databáze: JSTOR Journals