Expanded-access use of elamipretide in a critically ill patient with Barth syndrome

Autor: Goldstein, Amy C., Pantano, Cassandra, Redko, Mariya, MacMullen, Laura E., Maeda, Katsuhide, O’Connor, Matthew J.
Zdroj: In Genetics in Medicine Open 2024 2
Databáze: ScienceDirect