O07: Optimization of positive investigational outcomes in Barth syndrome using a combination of placebo-controlled, extended open-label, and natural history comparison studies*
| Autor: | Vernon, Hilary, Hornby, Brittany, Abbruscato, Anthony, Carr, Jim, Thompson, W. Reid |
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| Zdroj: | In Genetics in Medicine Open 2023 1(1) Supplement |
| Databáze: | ScienceDirect |
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