3 - Comparison of Outcomes in Patients with Cerebral Adrenoleukodystrophy (CALD) Receiving Elivaldogene Autotemcel (eli-cel; Lenti-D) Gene Therapy in Clinical Trials Versus Those Receiving Allogeneic Hematopoietic Stem Cell Transplant in a Contemporaneous Comparator Study

Autor: Duncan, Christine N., Kühl, Jörn-Sven, Chiesa, Robert, Boelens, Jaap-Jan, Eichler, Florian, Sevin, Caroline, Dalle, Jean-Hugues, De Oliveira, Satiro N., Amartino, Hernan M., Kapoor, Neena, Prasad, Vinod K., Jones, Simon, Algeri, Mattia, Bunin, Nancy J., Diaz-de-Heredia, Cristina, Thrasher, Adrian J., Fernandes, Juliana Folloni, Smith, Nicholas, Shah, Ami J, Locatelli, Franco, Engelen, Marc, Lindemans, Caroline A., Dietz, Andrew C., Pan, Lin, Sieker, Jakob, Williams, David A., Orchard, Paul J.
Zdroj: In Transplantation and Cellular Therapy March 2022 28(3) Supplement:S2-S4
Databáze: ScienceDirect
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