Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
| Autor: | Esposito, Federica, Dell’Aquila, Fabio, Rhiel, Manuel, Auricchio, Stefano, Chmielewski, Kay Ole, Andrieux, Geoffroy, Ferla, Rita, Horrach, Paula Sureda, Padmanabhan, Arjun, Di Cunto, Roberto, Notaro, Simone, Santeularia, Manel Llado, Boerries, Melanie, Dell’Anno, Margherita, Nusco, Edoardo, Padula, Agnese, Nutarelli, Sofia, Cornu, Tatjana I., Sorrentino, Nicolina Cristina, Piccolo, Pasquale, Trapani, Ivana, Cathomen, Toni, Auricchio, Alberto |
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| Zdroj: | In Cell Reports Medicine 16 July 2024 5(7) |
| Databáze: | ScienceDirect |
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