Prime editing functionally corrects cystic fibrosis-causing CFTR mutations in human organoids and airway epithelial cells
Autor: | Bulcaen, Mattijs, Kortleven, Phéline, Liu, Ronald B., Maule, Giulia, Dreano, Elise, Kelly, Mairead, Ensinck, Marjolein M., Thierie, Sam, Smits, Maxime, Ciciani, Matteo, Hatton, Aurelie, Chevalier, Benoit, Ramalho, Anabela S., Casadevall i Solvas, Xavier, Debyser, Zeger, Vermeulen, François, Gijsbers, Rik, Sermet-Gaudelus, Isabelle, Cereseto, Anna, Carlon, Marianne S. |
---|---|
Zdroj: | In Cell Reports Medicine 21 May 2024 5(5) |
Databáze: | ScienceDirect |
Externí odkaz: |