Rescue of infant progressive familial intrahepatic cholestasis type 3 mice by repeated dosing of AAV gene therapy

Autor: Weber, Nicholas D., Odriozola, Leticia, Ros-Gañán, Irene, García-Porrero, Guillermo, Salas, David, Argemi, Josepmaria, Combal, Jean-Philippe, Kishimoto, Takashi K., González-Aseguinolaza, Gloria
Zdroj: In JHEP Reports May 2023 5(5)
Databáze: ScienceDirect