BLEEDING RATE, FVIII UTILIZATION, CORTICOSTEROID USE, QUALITY OF LIFE AND SAFETY 4-YEARS AFTER GENE TRANSFER WITH VALOCTOCOGENE ROXAPARVOVEC IN A BRAZILIAN COHORT: RESULTS FROM GENER8-1

Autor: Ozelo, MC, Hayakawa, GGY, Prezotti, ANL, Cerqueira, MH, Villaça, PR, Lorenzatto, C, Robinson, T
Zdroj: In Hematology, Transfusion and Cell Therapy October 2024 46 Supplement 4:S575-S575
Databáze: ScienceDirect