EIGHTEEN-MONTH INTERIM ANALYSIS OF EFFICACY AND SAFETY OF GIVOSIRAN, AN RNAI THERAPEUTIC FOR ACUTE HEPATIC PORPHYRIA, IN THE ENVISION OPEN LABEL EXTENSION

Autor: Kuter, D, Keel, S, Parker, C, Rees, DC, Stölzel, U, Ventura, P, Balwani, M, Gouya, L, Rhyee, S, Silver, S
Zdroj: In Hematology, Transfusion and Cell Therapy October 2021 43 Supplement 1:S5-S6
Databáze: ScienceDirect