A PHASE 1/2 OPEN LABEL EXTENSION STUDY OF GIVOSIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC, IN PATIENTS WITH ACUTE INTERMITTENT PORPHYRIA

Autor: Marchi, R., Duarte, L., P, S., D, R., Ke, A., Hl, B., E, S., P, H., M, B., Al, E.
Zdroj: In Hematology, Transfusion and Cell Therapy November 2020 42 Supplement 2:17-18
Databáze: ScienceDirect