A simplified G-CSF–free procedure allows for in vivo HSC gene therapy of sickle cell disease in a mouse model

Autor: Li, Chang, Anderson, Anna K., Ruminski, Peter, Rettig, Michael, Karpova, Darja, Kiem, Hans-Peter, DiPersio, John F., Lieber, André
Zdroj: In Blood Advances 13 August 2024 8(15):4089-4101
Databáze: ScienceDirect