Transcutaneous ultrasound-mediated gene delivery into canine livers achieves therapeutic levels of factor VIII expression

Autor: Manson, Megan A. *, Zhang, Feng *, Novokhodko, Alexander, Chen, Chun-Yu, Parker, Maura, Loeb, Keith R., Kajimoto, Masaki, Campbell, Carley, Storb, Rainer F., Miao, Carol H. *
Zdroj: In Blood Advances 28 June 2022 6(12):3557-3568
Databáze: ScienceDirect