Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B

Autor: Von Drygalski, Annette, Giermasz, Adam, Castaman, Giancarlo, Key, Nigel S., Lattimore, Susan, Leebeek, Frank W.G., Miesbach, Wolfgang, Recht, Michael, Long, Alison, Gut, Robert, Sawyer, Eileen K., Pipe, Steven W.
Zdroj: In Blood Advances 12 November 2019 3(21):3241-3247
Databáze: ScienceDirect