A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis
| Autor: | Kell, Pamela, Sidhu, Rohini, Qian, Mingxing, Mishra, Sonali, Nicoli, Elena-Raluca, D'Souza, Precilla, Tifft, Cynthia J., Gross, Amanda L., Gray-Edwards, Heather L., Martin, Douglas R., Sena- Esteves, Miguel, Dietzen, Dennis J., Singh, Manmilan, Luo, Jingqin, Schaffer, Jean E., Ory, Daniel S., Jiang, Xuntian |
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| Zdroj: | In eBioMedicine June 2023 92 |
| Databáze: | ScienceDirect |
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