Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia

Autor: An, Ding, Frassetto, Andrea, Jacquinet, Eric, Eybye, Marianne, Milano, Joseph, DeAntonis, Christine, Nguyen, Vi, Laureano, Rodrigo, Milton, Jaclyn, Sabnis, Staci, Lukacs, Christine M., Guey, Lin T.
Zdroj: In EBioMedicine July 2019 45:519-528
Databáze: ScienceDirect