Preclinical ex vivo IL2RG gene therapy using autologous hematopoietic stem cells as an effective and safe treatment for X-linked severe combined immunodeficiency disease

Autor: Hu, Mingfeng, Xu, Qiling, Zhang, Fang, Buckland, Karen, Gao, Yelei, Du, Weixia, Ding, Yuan, Zhou, Lina, Sun, Xiulian, Ma, Lijia, Zhang, Zhiyong, Tang, Xuemei, Zhao, Xiaodong, Thrasher, Adrian J., An, Yunfei
Zdroj: In Genes & Diseases August 2024
Databáze: ScienceDirect