A novel class of self-complementary AAV vectors with multiple advantages based on cceAAV lacking mutant ITR

Autor: Zhang, Junping, Frabutt, Dylan A., Chrzanowski, Matthew, Li, Ning, Miller, Lohra M., Tian, Jiahe, Mulcrone, Patrick L., Lam, Anh K., Draper, Benjamin E., Jarrold, Martin F., Herzog, Roland W., Xiao, Weidong
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1)
Databáze: ScienceDirect