A novel class of self-complementary AAV vectors with multiple advantages based on cceAAV lacking mutant ITR
Autor: | Zhang, Junping, Frabutt, Dylan A., Chrzanowski, Matthew, Li, Ning, Miller, Lohra M., Tian, Jiahe, Mulcrone, Patrick L., Lam, Anh K., Draper, Benjamin E., Jarrold, Martin F., Herzog, Roland W., Xiao, Weidong |
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Zdroj: | In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1) |
Databáze: | ScienceDirect |
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