Comparative dose effectiveness of intravenous and intrathecal AAV9.CB7.hIDS, RGX-121, in mucopolysaccharidosis type II mice
| Autor: | Smith, Miles C., Belur, Lalitha R., Karlen, Andrea D., Erlanson, Olivia, Furcich, Justin, Lund, Troy C., Seelig, Davis, Kitto, Kelley F., Fairbanks, Carolyn A., Kim, Kwi Hye, Buss, Nick, McIvor, R. Scott |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1) |
| Databáze: | ScienceDirect |
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