Efficient and sustained FOXP3 locus editing in hematopoietic stem cells as a therapeutic approach for IPEX syndrome

Autor: Singh, Swati, Pugliano, Cole M., Honaker, Yuchi, Laird, Aidan, DeGottardi, M. Quinn, Lopez, Ezra, Lachkar, Stefan, Stoffers, Claire, Sommer, Karen, Khan, Iram F., Rawlings, David J.
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1)
Databáze: ScienceDirect