AAV-based gene therapy ameliorated CNS-specific GPI defect in mouse models
| Autor: | Murakami, Yoshiko, Umeshita, Saori, Imanishi, Kae, Yoshioka, Yoshichika, Ninomiya, Akinori, Sunabori, Takehiko, Likhite, Shibi, Koike, Masato, Meyer, Kathrin C., Kinoshita, Taroh |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1) |
| Databáze: | ScienceDirect |
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