Iron oxide-coupled CRISPR-nCas9-based genome editing assessment in mucopolysaccharidosis IVA mice

Autor: Leal, Andrés Felipe, Celik, Betul, Fnu, Nidhi, Khan, Shaukat, Tomatsu, Shunji, Alméciga-Díaz, Carlos Javier
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 December 2023 31
Databáze: ScienceDirect