Lethality rescue and long-term amelioration of a citrullinemia type I mouse model by neonatal gene-targeting combined to SaCRISPR-Cas9
| Autor: | Lisjak, Michela, Iaconcig, Alessandra, Guarnaccia, Corrado, Vicidomini, Antonio, Moretti, Laura, Collaud, Fanny, Ronzitti, Giuseppe, Zentilin, Lorena, Muro, Andrés F. |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 14 December 2023 31 |
| Databáze: | ScienceDirect |
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