CRISPR-Cas9 homology-independent targeted integration of exons 1–19 restores full-length dystrophin in mice
| Autor: | Stephenson, Anthony A., Nicolau, Stefan, Vetter, Tatyana A., Dufresne, Gabrielle P., Frair, Emma C., Sarff, Jessica E., Wheeler, Gregory L., Kelly, Benjamin J., White, Peter, Flanigan, Kevin M. |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:486-499 |
| Databáze: | ScienceDirect |
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