Molecular dynamics of genome editing with CRISPR-Cas9 and rAAV6 virus in human HSPCs to treat sickle cell disease

Autor: Xu, Liwen, Lahiri, Premanjali, Skowronski, Jason, Bhatia, Neehar, Lattanzi, Annalisa, Porteus, Matthew H.
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:317-331
Databáze: ScienceDirect