Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy

Autor: Le Guiner, Caroline, Xiao, Xiao, Larcher, Thibaut, Lafoux, Aude, Huchet, Corinne, Toumaniantz, Gilles, Adjali, Oumeya, Anegon, Ignacio, Remy, Séverine, Grieger, Josh, Li, Juan, Farrokhi, Vahid, Neubert, Hendrik, Owens, Jane, McIntyre, Maritza, Moullier, Philippe, Samulski, R. Jude
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:30-47
Databáze: ScienceDirect