iPSC-derived neural precursor cells engineering GBA1 recovers acid β-glucosidase deficiency and diminishes α-synuclein and neuropathology

Autor: Peng, Yanyan, Liou, Benjamin, Lin, Yi, Mayhew, Christopher N., Fleming, Sheila M., Sun, Ying
Zdroj: In Molecular Therapy - Methods & Clinical Development 8 June 2023 29:185-201
Databáze: ScienceDirect