GENE TARGET: A framework for evaluating Mendelian neurodevelopmental disorders for gene therapy

Autor: Chopra, Maya, Modi, Meera E., Dies, Kira A., Chamberlin, Nancy L., Buttermore, Elizabeth D., Brewster, Stephanie Jo, Prock, Lisa, Sahin, Mustafa
Zdroj: In Molecular Therapy - Methods & Clinical Development 8 December 2022 27:32-46
Databáze: ScienceDirect