Lentiviral gene therapy prevents anti-human acid α-glucosidase antibody formation in murine Pompe disease

Autor: Liang, Qiushi, Vlaar, Eva C., Catalano, Fabio, Pijnenburg, Joon M., Stok, Merel, van Helsdingen, Yvette, Vulto, Arnold G., Unger, Wendy W.J., van der Ploeg, Ans T., Pijnappel, W.W.M. Pim, van Til, Niek P.
Zdroj: In Molecular Therapy - Methods & Clinical Development 9 June 2022 25:520-532
Databáze: ScienceDirect