Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette

Autor: Kumar, Sandeep R.P., Xie, Jun, Hu, Shilang, Ko, Jihye, Huang, Qifeng, Brown, Harrison C., Srivastava, Alok, Markusic, David M., Doering, Christopher B., Spencer, H. Trent, Srivastava, Arun, Gao, Guangping, Herzog, Roland W.
Zdroj: In Molecular Therapy - Methods & Clinical Development 10 December 2021 23:98-107
Databáze: ScienceDirect