Systemic delivery of AAVrh74.tMCK.hCAPN3 rescues the phenotype in a mouse model for LGMD2A/R1
| Autor: | Sahenk, Zarife, Ozes, Burcak, Murrey, Darren, Myers, Morgan, Moss, Kyle, Yalvac, Mehmet E., Ridgley, Alicia, Chen, Lei, Mendell, Jerry R. |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 10 September 2021 22:401-414 |
| Databáze: | ScienceDirect |
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