Galactosialidosis: preclinical enzyme replacement therapy in a mouse model of the disease, a proof of concept
| Autor: | Cadaoas, Jaclyn 1, Hu, Huimin 2, 3, Boyle, Gabrielle 1, 3, Gomero, Elida 2, 3, Mosca, Rosario 2, 3, Jayashankar, Kartika 1, Machado, Mike 1, Cullen, Sean 1, Guzman, Belle 1, van de Vlekkert, Diantha 2, Annunziata, Ida 2, Vellard, Michel 1, Kakkis, Emil 1, Koppaka, Vish 1, d’Azzo, Alessandra 2, ∗ |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 12 March 2021 20:191-203 |
| Databáze: | ScienceDirect |
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