Unexpected Mutations by CRISPR-Cas9 CTG Repeat Excision in Myotonic Dystrophy and Use of CRISPR Interference as an Alternative Approach

Autor: Ikeda, Miki, Taniguchi-Ikeda, Mariko, Kato, Takema, Shinkai, Yasuko, Tanaka, Sonoko, Hagiwara, Hiroki, Sasaki, Naomichi, Masaki, Toshihiro, Matsumura, Kiichiro, Sonoo, Masahiro, Kurahashi, Hiroki, Saito, Fumiaki
Zdroj: In Molecular Therapy - Methods & Clinical Development 11 September 2020 18:131-144
Databáze: ScienceDirect