Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing

Autor: Erwood, Steven 1, 2, 6, Laselva, Onofrio 3, 4, 6, Bily, Teija M.I. 1, Brewer, Reid A. 1, Rutherford, Alexandra H. 1, Bear, Christine E. 3, 4, 5, Ivakine, Evgueni A. 1, 4, ∗
Zdroj: In Molecular Therapy - Methods & Clinical Development 12 June 2020 17:1118-1128
Databáze: ScienceDirect