Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia

Autor: Lidonnici, Maria Rosa, Paleari, Ylenia, Tiboni, Francesca, Mandelli, Giacomo, Rossi, Claudia, Vezzoli, Michela, Aprile, Annamaria, Lederer, Carsten Werner, Ambrosi, Alessandro, Chanut, Franck, Sanvito, Francesca, Calabria, Andrea, Poletti, Valentina, Mavilio, Fulvio, Montini, Eugenio, Naldini, Luigi, Cristofori, Patrizia, Ferrari, Giuliana
Zdroj: In Molecular Therapy - Methods & Clinical Development 14 December 2018 11:9-28
Databáze: ScienceDirect