Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
| Autor: | Yadak, Rana 1, 2, Cabrera-Pérez, Raquel 3, Torres-Torronteras, Javier 3, Bugiani, Marianna 4, Haeck, Joost C. 5, Huston, Marshall W. 1, Bogaerts, Elly 6, Goffart, Steffi 7, Jacobs, Edwin H. 6, Stok, Merel 2, 6, 8, Leonardelli, Lorena 9, Biasco, Luca 9, 10, 11, Verdijk, Robert M. 12, Bernsen, Monique R. 5, Ruijter, George 6, Martí, Ramon 3, Wagemaker, Gerard 2, 13, 14, 16, van Til, Niek P. 2, 15, 16, de Coo, Irenaeus F.M. 1, 16, ∗ |
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| Zdroj: | In Molecular Therapy - Methods & Clinical Development 16 March 2018 8:152-165 |
| Databáze: | ScienceDirect |
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