Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene

Autor: Vannoy, Charles Harvey, Xiao, Will, Lu, Peijuan, Xiao, Xiao, Lu, Qi Long
Zdroj: In Molecular Therapy - Methods & Clinical Development 16 June 2017 5:31-42
Databáze: ScienceDirect