Avalglucosidase alfa in infantile-onset Pompe disease: A snapshot of real-world experience in Italy
Autor: | Fiumara, Agata, Sapuppo, Annamaria, Gasperini, Serena, Crescitelli, Viola, Sacchini, Michele, Procopio, Elena, Gragnaniello, Vincenza, Burlina, Alberto |
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Zdroj: | In Molecular Genetics and Metabolism Reports September 2024 40 |
Databáze: | ScienceDirect |
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