Pegvaliase for the treatment of phenylketonuria: Final results of a long-term phase 3 clinical trial program

Autor: Harding, Cary O., Longo, Nicola, Northrup, Hope, Sacharow, Stephanie, Singh, Rani, Thomas, Janet A., Vockley, Jerry, Zori, Roberto T., Bulloch Whitehall, Kaleigh, Lilienstein, Joshua, Lindstrom, Kristin, Levy, Drew G., Jones, Shaun, Burton, Barbara K.
Zdroj: In Molecular Genetics and Metabolism Reports June 2024 39
Databáze: ScienceDirect