Cardiorespiratory management of Duchenne muscular dystrophy: emerging therapies, neuromuscular genetics, and new clinical challenges

Autor: Birnkrant, David J *, Bello, Luca, Butterfield, Russell J, Carter, John C, Cripe, Linda H, Cripe, Timothy P, McKim, Douglas A, Nandi, Deipanjan, Pegoraro, Elena
Zdroj: In The Lancet Respiratory Medicine April 2022 10(4):403-420
Databáze: ScienceDirect