Medical Costs Related to Enzyme Replacement Therapy for Mucopolysaccharidosis Types I, II, and VI in Brazil: A Multicenter Study

Autor: Bitencourt, Fernanda Hendges de, Vieira, Taiane Alves, Steiner, Carlos Eduardo, Neto, Jordão Correa, Boy, Raquel, Schwartz, Ida Vanessa Doederlein
Zdroj: In Value in Health Regional Issues December 2015 8:99-106
Databáze: ScienceDirect